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The California Stem Cell Report
FDA Hearing Tuesday: Off-target Risk Concerns for $2M Plus Proposed Genetic Treatment for Sickle Cell

FDA Hearing Tuesday: Off-target Risk Concerns for $2M Plus Proposed Genetic Treatment for Sickle Cell

Vertex and Crispr Therapetics working on therapy; California also has sickle cell trial underway

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David Jensen
Oct 29, 2023
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The California Stem Cell Report
FDA Hearing Tuesday: Off-target Risk Concerns for $2M Plus Proposed Genetic Treatment for Sickle Cell
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It will be a historic Halloween this week for a couple of companies hoping to turn their genetic experimentation into a successful $2 million-plus treatment for sickle cell disease. At least that is the view of one biotech news outlet. 

The matter involves Vertex Pharmaceuticals, Inc., of Boston, and Crispr Therapeutics, of Zug, Switzerland, and an advis…

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